This is the accessible text file for GAO report number GAO-07-996 
entitled 'Medical Devices: FDA's Approval of Four Temporomandibular 
Joint Implants' which was released on October 17, 2007. 

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Report to Congressional Requesters: 

United States Government Accountability Office: 

GAO: 

September 2007: 

Medical Devices: 

FDA's Approval of Four Temporomandibular Joint Implants: 

FDA's Approval of TMJ Implants: 

GAO-07-996: 

GAO Highlights: 

Highlights of GAO-07-996, a report to congressional requesters. 

Why GAO Did This Study: 

It is estimated that over 10 million people in the United States suffer 
from jaw joint and muscle disorders. Artificial temporomandibular joint 
(TMJ) implants have been used to replace the jaw joint in some patients 
in an effort to decrease pain and increase jaw function. The safety and 
effectiveness of these implants, like other medical devices, is 
overseen by the Food and Drug Administration (FDA), an agency within 
the Department of Health and Human Services (HHS). Two implants used in 
the 1970s and 1980s that were later removed from the market caused 
severe side effects for some patients. In 1998, FDA began to require 
certain TMJ implant manufacturers sponsoring these devices to 
demonstrate the implants’ safety and effectiveness before receiving 
approval. Since 1998, four TMJ implants from three sponsors were 
approved. 

In response to your request, GAO described (1) the types of concerns 
raised by FDA and how it addressed these concerns for the implants 
approved since 1998 and (2) how FDA has monitored sponsors’ compliance 
with conditions of approval. GAO examined documentation related to the 
four TMJ implants approved by FDA since 1998 and sponsors’ annual 
reports, which FDA uses to monitor compliance with conditions of 
approval. GAO also interviewed FDA officials, TMJ implant sponsors, and 
patient advocacy groups. 

What GAO Found: 

FDA officials raised concerns during the approval process that were 
similar for all four TMJ implants. These concerns generally involved 
the adequacy of the sponsors’ clinical study protocols, patient follow-
up, engineering testing, and other matters, such as device labeling. 
FDA addressed many, but not all, concerns upon approval. Some concerns 
were addressed by obtaining additional information from sponsors to 
clarify and supplement data contained in their device applications 
before approval. Other concerns were addressed when FDA approved the 
implants but required sponsors to comply with certain conditions of 
approval, such as continuing clinical studies postmarket and collecting 
patient data. Because FDA staff, who review the device applications, 
and FDA management, who approve the devices for marketing, held 
differing views as to whether the implants’ health benefits outweighed 
its risks, they did not agree on the approval decisions of two of the 
four TMJ implants. FDA management acknowledged that the concerns raised 
about the implants were legitimate. However, they ultimately concluded 
that the benefits provided by these two devices outweighed the concerns 
and approved both devices to help patients obtain relief from chronic 
pain. 

FDA monitored sponsors’ compliance with conditions of approval by 
evaluating information contained in their annual reports. FDA often 
required additional actions by the sponsors to resolve questions that 
were raised through its review of these reports. However, GAO found 
that not all annual reports were received by FDA. At the time GAO 
conducted its work, FDA had only received 13 of 18 required reports. 
One implant sponsor did not submit 5 of 7 required annual reports. FDA 
has requested these reports and has issued draft guidance on annual 
report submissions to all medical device sponsors. In addition, when 
reviewing the available annual reports to determine if sponsors were 
complying with conditions of approval, many of the submitted reports 
did not provide FDA with sufficient information to assess compliance. 
FDA required these TMJ implant sponsors to provide additional 
information to address this lack of sufficient information. In most 
instances, once FDA received additional information from the sponsors, 
the annual reports were considered adequate. However, one sponsor 
submitted several annual reports for both of its devices that FDA said 
lacked sufficient information regarding patient follow-up and also 
underreported problems experienced by patients associated with the 
devices. FDA notified the sponsor that it must address these concerns, 
but the sponsor repeatedly provided inadequate responses. This 
situation ultimately led FDA to inspect the sponsor’s records and file 
an administrative complaint for civil monetary penalties against the 
sponsor for failure to file certain reports with FDA. On July 6, 2007, 
an administrative law judge ruled in favor of FDA. 

In commenting on a draft of this report, HHS provided clarification on 
postmarket requirements for approved devices and updated information on 
the administrative complaint for civil monetary penalties. 

[hyperlink, http://www.gao.gov/cgi-bin/getrpt?GAO-07-996]. 

To view the full product, including the scope and methodology, click on 
the link above. For more information, contact Marcia Crosse at (202) 
512-7114 or crossem@gao.gov 

[End of section] 

Contents: 

Letter: 

Results in Brief: 

Background: 

FDA Raised Concerns on All Implants and Addressed Many by Obtaining 
Additional Information and Establishing Conditions of Approval: 

FDA Monitored Compliance through Review of the Sponsors' Annual Reports 
It Received and Required Some Sponsors to Take Additional Action: 

Agency Comments: 

Appendix I: Concerns Left Unaddressed upon FDA Approval of TMJ 
Implants: 

Appendix II: Comments from the Department of Health and Human Services: 

Appendix III: GAO Contact and Staff Acknowledgments: 

Tables: 

Table 1: GAO Categorization of Concerns Raised by FDA during the PMA 
Process for TMJ Implants: 

Table 2: GAO Categorization of Concerns Left Unaddressed by FDA during 
the Premarket Approval Process for TMJ Implants: 

Figure: 

Figure 1: Illustration of Temporomandibular Joint: 

Abbreviations: 

FDA: Food and Drug Administration: 
HHS: Department of Health and Human Services: 
MAUDE: Manufacturer and User Facility Device Experience Database: 
PMA: premarket approval TMJ temporomandibular joint: 

United States Government Accountability Office: 

Washington, DC 20548: 

September 17, 2007: 

The Honorable Edward M. Kennedy: 
Chairman: 
Committee on Health, Education, Labor, and Pensions: 
United States Senate: 

The Honorable Tom Harkin: 
United States Senate: 

The Honorable Herb Kohl: 
United States Senate: 

The National Institutes of Health report that over 10 million people in 
the United States suffer from temporomandibular joint (i.e., jaw joint) 
and muscle disorders. Although most people have relatively mild forms 
of these disorders, others experience long-term persistent and 
debilitating pain. Artificial temporomandibular joint (TMJ) implants 
have been used to replace the jaw joint in an effort to decrease pain 
and increase jaw function for this latter group. 

The Food and Drug Administration (FDA), an agency within the Department 
of Health and Human Services (HHS), is responsible for overseeing the 
safety and effectiveness of medical devices, including TMJ implants. 
Beginning in 1976, medical devices, including TMJ implants, were 
allowed to enter the market without the submission of safety and 
effectiveness information to FDA if the devices were determined to be 
"substantially equivalent" to previously marketed devices.[Footnote 1] 
Many patients who received certain TMJ implants--one that was on the 
market prior to 1976 and one that entered the market in 1983 and was 
deemed substantially equivalent to a pre-1976 device--faced severe 
consequences associated with the materials contained in the implants. 
These included chronic pain, bone degeneration, and implant 
fragmentation or displacement. In 1991, one device was recalled by FDA, 
and in 1993, the other was voluntarily discontinued by the 
manufacturer--who is also known as the sponsor--of the implant. 

On December 30, 1998, FDA issued regulations requiring certain TMJ 
implant sponsors to submit a premarket approval (PMA) application. 
Applications were required for TMJ implants marketed prior to May 28, 
1976, and for such implants deemed substantially equivalent to a device 
marketed prior to May 28, 1976. The PMA process requires sponsors to 
demonstrate the safety and effectiveness of their devices before 
receiving approval. To demonstrate safety and effectiveness of these 
devices, sponsors conduct clinical studies and perform engineering 
tests on the implant, such as testing the implant's strength, and 
include the results in the PMA application submitted for FDA's review. 
As part of the PMA process, FDA staff evaluate these studies through a 
review of the implant applications, and FDA management makes decisions 
regarding approval for marketing the implants. Since the implementation 
of these requirements, four TMJ implant applications from three 
sponsors have been submitted for approval. FDA conditionally approved 
all four devices--meaning the sponsors had to comply with specific 
conditions established by FDA, following approval. For example, these 
sponsors were required to conduct postmarket studies, among other 
conditions. Given your concerns for patients with temporomandibular 
joint and muscle disorders, you expressed interest in FDA's safety 
requirements for, and oversight of, TMJ implants. 

This report examines (1) the types of concerns raised by FDA and how it 
addressed concerns raised during the TMJ implant approval process since 
December 30, 1998, when it began requiring data on implant safety and 
effectiveness and (2) how FDA has monitored TMJ sponsors' compliance 
with conditions of approval. 

To determine how FDA addressed the concerns raised during the PMA 
process, we reviewed documentation provided by FDA for each of the four 
TMJ implants approved since December 30, 1998: (1) TMJ Concepts 
implant, (2) TMJ Implants, Inc., total joint implant, (3) TMJ Implants, 
Inc., partial joint implant, and (4) Walter Lorenz implant.[Footnote 2] 
We identified FDA's concerns related to safety and effectiveness and 
the methods used to address these concerns through a review of internal 
documents, such as the approval review package. Among other documents, 
this package includes results of FDA's reviews of the PMA application, 
a recommendation regarding approval, and final decisions for each 
implant. Throughout our review we considered concerns addressed by FDA 
as those in which the agency identified an issue concerning safety and 
effectiveness of an implant and dealt with the issue by contacting the 
sponsor. We also reviewed FDA's correspondence with the TMJ implant 
sponsors. In addition, to further understand FDA's concerns, we 
examined summaries of meetings held by FDA's dental products panel--an 
advisory body of external experts convened to provide advice to the 
agency--on each of the four PMA applications. An FDA official indicated 
that although the agency may not have documentation of all concerns 
raised during the PMA process, the documents we reviewed contained the 
most complete information possible to address our objectives. 
Therefore, it is possible that other relevant documents existed that we 
were unable to review. We grouped concerns raised during the PMA 
process into broad categories, such as study protocol, patient follow- 
up, and engineering testing.[Footnote 3] In addition, we further sorted 
these categories to provide additional explanations on the types of 
concerns we identified. We also identified actions taken by FDA such as 
whether FDA approved the device with conditions to address certain 
concerns. We discussed our determinations of whether and how concerns 
were addressed with FDA officials to gain their confirmation. However, 
we did not evaluate the appropriateness of FDA's approval decisions for 
each of the implants or its assessment of the medical, scientific, or 
engineering data provided by the sponsors. To better inform our 
discussion of concerns raised during the PMA process for TMJ implants, 
we contacted the three TMJ implant sponsors[Footnote 4] and several 
groups representing patients with temporomandibular joint and muscle 
disorders, including the TMJ Association, the TMJ and Orofacial Pain 
Society of America, and the Jaw Joints & Allied Musculo-Skeletal 
Disorders Foundation, Inc. 

To determine how FDA has monitored TMJ implant sponsors' compliance 
with the conditions of approval, we reviewed annual reports, which FDA 
required from the three TMJ implant sponsors as a condition of 
approval. Among other things, these annual reports provide the sponsors 
an opportunity to update FDA on the status of their required conditions 
of approval. We discussed the status of conditions of approval with FDA 
officials to obtain their views on sponsors' compliance with these 
conditions and collected related documentation. In addition, we 
gathered information related to FDA's overall efforts to collect and 
review annual reports. With the exception of FDA's review of annual 
reports, this report focuses on how FDA addressed concerns raised 
during the PMA process and excludes FDA's postmarket oversight 
activities.[Footnote 5] 

Through our interviews with FDA officials and our examination of 
documents provided, we determined that the data we used were 
sufficiently reliable for purposes of this report. We conducted our 
review from October 2006 through August 2007 in accordance with 
generally accepted government auditing standards. 

Results in Brief: 

FDA officials raised similar concerns for all four TMJ implants' PMA 
applications. We grouped these concerns into four main categories: 
study protocol, patient follow-up, engineering testing, and other 
concerns, such as device labeling. For example, FDA found that all the 
studies supporting the four PMA applications had deficient patient 
follow-up, which made it difficult to determine outcomes over time, 
such as improvement in patient symptoms. FDA used two methods to 
address many, but not all, concerns upon approval. FDA addressed some 
concerns raised in the approval process by obtaining additional 
information from sponsors to clarify and supplement data contained in 
their PMA applications before approval. FDA addressed other concerns by 
approving the TMJ implants but requiring sponsors to comply with 
certain conditions of approval. As a condition of approval, FDA 
required the sponsors to continue their clinical studies postmarket and 
to collect data on patients for all four implants for at least 3 years. 
Because FDA staff, who review the device applications, and FDA 
management, who approve the devices for marketing, held differing views 
as to whether an implant's health benefits outweighed its risks, they 
did not agree on the approval decisions of two of the four TMJ 
implants, both sponsored by TMJ Implants, Inc. Ultimately, both devices 
were approved. FDA management acknowledged that the concerns raised 
about these implants were legitimate; however, they concluded that the 
need for the devices outweighed these concerns. According to FDA 
management, they approved the devices primarily because they play an 
important role in helping patients obtain relief from chronic pain and 
there did not appear to be a prohibitory risk associated with the 
devices. 

FDA monitored sponsors' compliance with conditions of approval by 
evaluating information contained in their annual reports and often 
required additional actions by the sponsors to resolve questions raised 
through its review of the reports. Although a total of 18 annual 
reports should have been submitted to FDA at the time we conducted our 
work, only 13 had been received by the agency. One implant sponsor--TMJ 
Concepts--did not submit 5 of 7 required annual reports. FDA has since 
requested these reports and has issued draft guidance to all medical 
device sponsors, which outlines best practices for submitting annual 
reports. When reviewing the annual reports from all of the sponsors to 
determine if conditions of approval were met, we found that 7 of the 13 
submitted reports did not provide FDA with sufficient information to 
assess compliance. To address the lack of sufficient data provided in 
these 7 annual reports, specifically with regard to patient history and 
patient follow-up, FDA contacted the sponsors and required them to 
provide additional information. TMJ Implants, Inc., submitted several 
annual reports for both of its devices that lacked sufficient 
information regarding patient follow-up. In addition, FDA said the 
sponsor also underreported problems experienced by patients--known as 
adverse events--associated with the devices. FDA issued letters to the 
sponsor asking it to resolve these concerns, yet the sponsor repeatedly 
provided inadequate responses. This situation ultimately led FDA to 
file an administrative complaint for civil monetary penalties against 
the sponsor, which resulted in a decision from an administrative law 
judge in favor of FDA on July 6, 2007. A separate decision is expected 
on the amount of the penalties to be assessed, after which either side 
may appeal. 

In commenting on a draft of this report, HHS provided clarification on 
the postmarket requirements that apply to approved devices. In 
addition, it updated information concerning the administrative 
complaint for civil monetary penalties. 

Background: 

Symptoms of temporomandibular joint and muscle disorders vary but 
typically include pain of the jaw joint and surrounding muscles. Other 
symptoms include limited or no movement of the jaw joint, clicking or 
grating in the jaw joint when opening or closing the mouth, headaches, 
and shoulder or back pain. According to the National Institutes of 
Health, most patients' symptoms improve significantly or disappear 
within weeks or months, while a smaller number of patients have 
significant long-term symptoms. Trauma to the jaw or jaw joint can 
contribute to temporomandibular joint and muscle disorders in some 
instances; however, the causes of most cases of temporomandibular joint 
and muscle disorders are unknown. 

There are a range of treatments available for temporomandibular joint 
and muscle disorders; some are conservative and temporary while others 
are irreversible. Experts recommend that the most conservative 
treatment be used to relieve symptoms before irreversible treatments 
are used. Conservative treatments can include taking pain medications, 
using a splint or bite guard, applying ice packs, or eating soft food. 
Irreversible treatments include grinding down the teeth to change a 
person's bite or surgical procedures such as replacing all or a portion 
of the jaw joint with TMJ implants. Total TMJ implants replace both the 
upper (articular fossa) and lower (condyle) portions of the jaw joint, 
whereas partial TMJ implants replace only the upper portion. (See fig. 
1.) TMJ implants may improve the function of the jaw joint, however, 
pain, which is a chief complaint of many who suffer from 
temporomandibular joint and muscle disorders, is not always relieved. 

Figure 1: Illustration of Temporomandibular Joint: 

[See PDF for image] 

Source: Reprinted with permission from the American Association of Oral 
and Maxillofacial Surgeons. 

[End of figure] 

Medical devices, including TMJ implants, are regulated by FDA, through 
its Center for Devices and Radiological Health. TMJ implants are 
classified as Class III devices. Class III devices include those that 
present a significant risk of illness or injury to the 
patient.[Footnote 6] 

Prior to the marketing of most Class III devices, FDA must approve a 
PMA application.[Footnote 7] The PMA review requires sufficient and 
valid scientific evidence to assure that a medical device is safe and 
effective for its intended use. In making this determination, FDA 
officials--including FDA staff known as the review team[Footnote 8] and 
two levels of FDA management--must consider if there is reasonable 
assurance that the probable benefits to health of the device outweigh 
any probable risks. They must also consider whether the device is 
effective by evaluating data provided by the sponsor for "clinically 
significant results."[Footnote 9] The review team examines clinical 
studies of the device involving human subjects, engineering testing 
performed on the device, and other aspects of the PMA application such 
as device labeling. It may also obtain input from one of its external 
advisory boards--in the case of TMJ implants, its dental products 
panel--for its evaluation and recommendation regarding approval. If the 
review team has concerns about the PMA application it contacts the 
sponsor for more information.[Footnote 10] In some cases the review 
team may determine that it needs significant additional information to 
complete the scientific review, in which case it issues a deficiency 
letter to the device sponsor indicating the information that is needed. 
The sponsor can respond by submitting an amendment to the original 
application. The review team can continue to issue deficiency letters 
and receive amendments from sponsors until it determines that it has 
the information needed to make a recommendation regarding approval. 

Once the PMA review is complete, the review team makes a recommendation 
regarding approval. This recommendation is subject to review by the two 
levels of FDA management. Along with the recommendation, information 
provided by the sponsor and the review team's assessment of the PMA 
application, including the individual reviews, such as engineering, 
clinical, and statistical reviews, and a team leader summary, are 
forwarded. The review team sends this package to the first level of 
management. If this level of management agrees with the review team's 
recommendation, the review package is sent to the second level for 
final review.[Footnote 11] The second level of management may concur or 
override the decision made at the previous management level. Management 
can make a recommendation regarding approval even if some concerns 
regarding the PMA remain unaddressed; however, a device can only be 
approved for marketing if FDA concludes that its benefits outweigh its 
risks. If a member of the review team or the first level of FDA 
management disagrees with the final decision, an internal "respectful 
disagreement memo" can be written indicating the reason for the 
disagreement.[Footnote 12] 

FDA decisions regarding approval of devices can take four forms: (1) 
issuing an order approving the application, which allows the sponsor to 
begin marketing the device; (2) sending the sponsor an "approvable" 
letter indicating that the sponsor needs to provide more information; 
(3) issuing a "not approvable" letter informing the sponsor of the 
application's weaknesses; or (4) issuing an order denying approval of 
the application. 

Once a device has been approved, the sponsor must comply with 
postmarket regulations and restrictions that apply to the device. FDA 
may also impose postmarket approval or condition of approval 
requirements that apply specifically to the device that is the subject 
of the PMA. Conditions of approval can include requirements such as the 
continuation of a clinical study to collect additional data. Some 
conditions of approval do not expire, such as reporting adverse events 
and submitting annual reports, including a summary of all changes to 
the device.[Footnote 13] Others are time-limited, such as continuing a 
clinical study for a specified number of years after the approval of a 
device. 

FDA Raised Concerns on All Implants and Addressed Many by Obtaining 
Additional Information and Establishing Conditions of Approval: 

In their review of the four PMA applications, FDA officials raised 
concerns that were similar for all four devices. FDA addressed many 
concerns raised in the approval process by obtaining additional 
information from sponsors to clarify and supplement data contained in 
their PMA applications. It also approved all four devices but required 
sponsors to comply with conditions of approval. However, some concerns 
were left unaddressed upon approval. In addition, the FDA review team 
and two levels of FDA management did not agree on the assessment of the 
safety and effectiveness of the two TMJ Implants, Inc., devices. 
Ultimately, according to FDA management, the primary justification for 
approving these devices was that the potential benefit to the patients 
outweighed the concerns raised and there did not appear to be a 
prohibitory risk associated with the devices. 

FDA Raised Concerns That Generally Applied to All Four TMJ Implants: 

We grouped the concerns FDA raised during the PMA process into four 
main categories: study protocol, patient follow-up, engineering 
testing, and other concerns. These categories and types of concerns are 
shown in table 1. 

Table 1: GAO Categorization of Concerns Raised by FDA during the PMA 
Process for TMJ Implants: 

Categories of concerns: Study protocol; 
Types of concerns included in categories: 
* Inadequate or inaccurate clinical study results, including: 
- Inaccurate measurement of data (e.g., problems with procedures used 
to measure pain over time)[A]; 
- Data not separated appropriately (e.g., results from different 
implants analyzed together)[A]; 
- Questionable conduct by sponsor (e.g., underreporting of adverse 
events)[A]; 
- Incomplete or insufficient data to draw conclusions[A]; 
- Lack of long-term data collection[A]; 
- Unsupported or poorly defined indications for use[A]; 
* Lack of patient history data, including: 
- Patients' clinical diagnosis unknown (e.g., rheumatoid arthritis, 
cancer)[A]; 
- Patients' treatment history unknown (e.g., first implant, multiple 
implants); 
- Original sample size of study too small. 

Categories of concerns: Patient follow-up[B]; 
Types of concerns included in categories: 
* Lack of patient follow-up, including: 
- Long-term data lacking due to poor follow-up[A]; 
- Number of patients in study too small due to poor follow-up[A]. 

Categories of concerns: Engineering testing; 
Types of concerns included in categories: 
* Inadequate wear testing, including: 
- Analysis of wear debris from implant lacking[A]; 
- No examination for wear of implants removed from patients[A]; 
- No analysis of wear on natural condyle[A,C]; 
* Inadequate fatigue testing[A,D]; 
* Other engineering testing inadequate[A]. 

Categories of concerns: Other; 
Types of concerns included in categories: 
* Inadequate device labeling[A]; 
* Unaddressed microbiology,[E] packaging, and shelf-life issues; 
* Incomplete sponsor manufacturing inspections. 

Source: GAO analysis of FDA documents. 

Notes: This table applies to the four TMJ implants approved since 
December 30, 1998. 

[A] These concerns were also raised by the dental products panel in its 
review of the PMA applications for the four implants. 

[B] Patient follow-up refers to the number of patients who remain in a 
study over time. 

[C] The TMJ Concepts, TMJ Implants, Inc., total implant, and Walter 
Lorenz implants replace both the articular fossa (the upper portion of 
the temporomandibular joint) and the condyle (the lower portion). The 
TMJ Implants, Inc., partial implant only replaces the articular fossa, 
therefore there were concerns related to its effects on a patient's 
natural condyle. 

[D] Fatigue testing refers to the amount of weight an implant can bear 
without breaking. Tests are conducted to ensure that the implant can 
withstand the weight that a functioning jaw joint would encounter 
during activities such as talking and chewing. 

[E] Microbiology issues relate to the sponsors' processes to ensure the 
devices are sterile when shipped to the device user. 

[End of table] 

From FDA's review of the PMA applications, we observed similar concerns 
across most PMA applications. For example: 

* All four PMA applications had incomplete or insufficient data to draw 
conclusions from the clinical studies. For example, FDA officials were 
concerned that because the Walter Lorenz clinical study was primarily 
conducted at one site, the physician at this site might have more 
expertise in implanting the device than a typical physician, 
potentially biasing the results. Officials were uncertain if equally 
favorable results would be obtained at other sites when the implant 
procedure was performed by less-experienced physicians. 

* All four PMA applications had deficient patient follow-up 
information, which prevented a satisfactory evaluation of the study 
results, such as improvement in patient symptoms and survivability of 
the implant.[Footnote 14] 

* In three of the four PMA applications, concerns were raised about the 
lack of information specifying the clinical diagnosis of the patients 
included in their clinical studies. This made it difficult for the 
review team to interpret the types of clinical conditions for which the 
devices are appropriate. 

* In three of the four PMA applications, concerns existed regarding 
inaccurate measurement of data. For example, neither TMJ Concepts's nor 
TMJ Implants, Inc.'s, total implant clinical data followed the same 
cohort of patients over time. This made it difficult for the review 
team to determine whether the device produced improvements in patients. 
The clinical data for TMJ Implants, Inc.'s, partial implant were 
compromised because medications used by patients were not documented in 
the study. Any use of medications could have affected patient outcomes. 

* In three of the four PMA applications, the review team indicated that 
additional implant wear and fatigue testing needed to be conducted. For 
example, the team wanted TMJ Implants, Inc., (total implant) to conduct 
wear debris analysis. This analysis could help determine if material 
wears off the implant over time, which could be absorbed into the 
patient's body. 

FDA Obtained Additional Information from Sponsors and Required 
Conditions of Approval to Address Most, but Not All, Concerns: 

FDA addressed the concerns it raised in its review of the PMA 
applications in two ways: (1) by communicating with sponsors and 
collecting additional information from them and (2) by approving the 
devices with conditions. FDA addressed many of its concerns by 
clarifying and collecting information for sponsors' PMA applications, 
before approving the devices. For example, FDA officials met with 
representatives of TMJ Concepts and TMJ Implants, Inc., (partial 
implant) to discuss concerns, such as unsupported indications for use 
of the device and inconsistent patient follow-up in the clinical 
studies. In addition, in many instances throughout the review process, 
FDA officials wrote the sponsors--highlighting problems with the 
applications--and reviewed their written responses. For example, FDA 
sent e-mails to Walter Lorenz regarding concerns related to the 
microbiology, packaging, and shelf life of its device. Walter Lorenz 
replied to FDA's questions and requests for information and these 
concerns were addressed. Correspondence between FDA officials and 
sponsors often continued for at least 3 months and in most cases longer 
until concerns were addressed. 

The second manner in which FDA addressed concerns was by approving the 
four TMJ implants with certain conditions. A condition of approval 
common to all four TMJ implants included the requirement that a 
postmarket study be conducted, which would collect patient data for at 
least 3 years. This condition of approval addressed FDA's concerns 
regarding study protocol and patient follow-up. Other conditions of 
approval addressed concerns related to a lack of patient history data 
and inadequate wear testing, among others. TMJ Concepts and TMJ 
Implants, Inc., (total implant) were required to include patient 
history data in their postmarket studies. Further, TMJ Concepts and TMJ 
Implants, Inc., (partial implant) were required to conduct wear 
analysis in order to address concerns related to inadequate wear 
testing. 

While FDA addressed the majority of concerns for each implant, we 
identified some concerns that remained unaddressed--concerns that were 
not offset or countered by a condition of approval or by FDA 
correspondence with the sponsor--upon approval. FDA officials examined 
these unaddressed concerns during the PMA process. However, they 
determined that the probable benefits of the devices outweighed the 
probable risks and therefore approved them. The unaddressed concerns 
for the devices were as follows and are expanded upon in appendix I: 

* TMJ Concepts: The unaddressed concerns related to inadequate and 
inaccurate study results. For example, FDA officials indicated that 
data for implants on the right and left sides of the jaw should have 
been analyzed separately, but the data collected did not allow for this 
type of analysis. 

* TMJ Implants, Inc. (total implant): The unaddressed concerns related 
to the category of other concerns--unaddressed microbiology, packaging, 
and shelf-life issues. For example, there was a concern regarding the 
procedures used for implants that will be shipped multiple times, which 
could occur if a physician shipped an unused implant back to the 
sponsor. 

* TMJ Implants, Inc. (partial implant): The majority of the unaddressed 
concerns related to inadequate and inaccurate study results and lack of 
patient history data. For example, there were concerns that the 
indications for use the sponsor cited in the device labeling were not 
supported by the clinical study. In addition, information about 
patients' treatment history was not included in the study, so it was 
unknown whether patients tried more conservative treatments before 
receiving the device. The remaining unaddressed concerns related to 
other topics--unaddressed microbiology, packaging, and shelf-life 
issues and outstanding manufacturing inspection matters. 

* Walter Lorenz: The unaddressed concern related to lack of patient 
history data, specifically that the sponsor generalized the clinical 
study results to all patients, even though patients in the study had 
varying clinical histories. 

Concerns Raised about Two Implants Resulted in Differing Opinions among 
FDA Officials Regarding Approval: 

Although FDA's review team and FDA management agreed that the TMJ 
Concepts and Walter Lorenz implants should be approved with conditions, 
there was disagreement among the review team and the two levels of 
management related to the approval of both TMJ Implants, Inc., devices. 
The review team recommended that the TMJ Implants, Inc., (total 
implant) application be considered not approvable. The team had 
concerns because it felt that the enrollment in the sponsor's clinical 
study was too small to draw significant conclusions related to the 
safety and effectiveness of the device. In addition, the review team 
believed the indications for use of the device were unsupported. 
However, the first level of FDA management recommended that the device 
be approved because it has a role in the treatment of TMJ and muscle 
disorders. The second level of management agreed with this 
recommendation. In its approval decision, FDA management acknowledged 
that there were concerns about the quality and quantity of clinical 
data provided by the sponsor. However, it stated that either good 
engineering data or good clinical data was acceptable to approve a 
device--not necessarily both--and that it deemed the engineering data 
for the TMJ Implants, Inc., total implant to be satisfactory. Further, 
FDA management indicated that the clinical data were not expected to be 
of high quality because the sponsor was a small manufacturer, the data 
available at the time of approval did not indicate an extraordinary 
problem with the implanted devices, and the data provided appeared 
consistent and favorable. The total implant was approved with 
conditions to address the FDA review team's concerns mentioned above. 

There was also conflict regarding the decision to approve the TMJ 
Implants, Inc., (partial implant) application. Although the second 
level of management ultimately approved the device for marketing with 
conditions, both the FDA review team and first level of management 
found that there was insufficient data to assure that the device was 
safe and effective. The review team recommended that the device be 
considered not approvable. The first level of management agreed with 
this recommendation for the following reasons: 

* The data were limited due to lack of patient follow-up. For example, 
the group of patients with 2-year and 3-year follow-up data in the 
sponsor's clinical study was too small to draw significant conclusions 
about the device. Of approximately 100 patients with implants, only 29 
completed the 24-month follow-up. Only 11 patients completed the 
intended 36-month follow-up. 

* Outstanding concerns existed related to (1) questionable conduct by 
the sponsor in classifying and reporting adverse events, (2) lack of 
engineering testing to determine the long-term effect of the partial 
TMJ implant on the natural condyle, (3) unsupported indications for use 
of the device, and (4) lack of data on patients' clinical and treatment 
history. 

While the second level of management recognized and agreed with the 
scientific concerns that had been raised, the sponsor was sent an 
approvable letter requiring minor application changes, such as revised 
device labeling, and the device was eventually approved. An internal 
memo outlining the second level of management's approval decision 
stated that there was a compelling argument in favor of approving the 
device. It argued that there appeared to be a small group of patients, 
although poorly defined, for whom the device seemed to provide an 
option for relief of chronic pain. In addition, it noted that there did 
not appear to be a prohibitory risk associated with the device in 
patients who are appropriately educated about all treatment 
alternatives, their disorder, and the device, and this information is 
provided in the implant's labeling. However, the approval memo also 
stated that the decision to approve the partial implant did not imply 
that the previous concerns raised by the review team and first level of 
management related to the inadequacy of the data were reversed. Of 
these concerns raised, those related to engineering testing on the 
device's effect on the natural condyle were addressed through 
conditions of approval; the others remained unaddressed. 

Upon the approval of the partial implant, two individuals--a member of 
the review team and an official from the first level of FDA management-
-wrote "respectful disagreement memos." Their memos indicated that they 
did not agree with the second level of management's decision to approve 
the TMJ implants, Inc., (partial implant) application for marketing. 
These memos outlined concerns raised during the PMA process related to 
the safety and effectiveness of the device. The concerns highlighted in 
these memos were that (1) lack of patient follow-up in the clinical 
study potentially biased the results, and consequently, the sponsor's 
claim that the implant resulted in decreased patient pain was 
unsupported, (2) the clinical study protocol lacked scientific rigor, 
and (3) outstanding questions remained related to the indications for 
using the device. In addition, a member of the review team told us that 
the conditions of approval did not mitigate the concerns she 
highlighted in her respectful disagreement memo. 

FDA Monitored Compliance through Review of the Sponsors' Annual Reports 
It Received and Required Some Sponsors to Take Additional Action: 

In order to evaluate how the sponsors complied with the conditions of 
approval, FDA received and reviewed the majority of the required annual 
reports from TMJ implant sponsors. However, the review team had not 
received most of the required annual reports from one sponsor. Of the 
annual reports the review team evaluated, some of them were incomplete 
and FDA required sponsors to take additional actions to ensure 
compliance with conditions of approval. In addition, the FDA review 
team had concerns about one sponsor's--TMJ Implants, Inc.--annual 
reports. FDA found that these reports lacked sufficient information 
that prevented them from monitoring safety and effectiveness. This 
eventually led FDA to investigate the sponsor, resulting in the 
subsequent filing of an administrative complaint for civil monetary 
penalties for the company's failure to file certain adverse event 
reports with FDA. 

FDA Reviewed the Annual Reports It Received, but Some Were Missing: 

FDA received and reviewed all required annual reports for TMJ Implants, 
Inc., total and partial implants between 2002 and 2006 and the Walter 
Lorenz implant in 2006. However, the review team was missing five of 
seven required annual reports between 2000 and 2006 from TMJ Concepts. 
It was not until we requested to review these reports that FDA 
contacted the sponsor to obtain the missing information. In addition, 
FDA officials told us that they are developing an improved postmarket 
surveillance effort to assist sponsors with annual report submission. 
As part of this effort, FDA recently issued draft guidance on October 
26, 2006, which outlines FDA's recommendations for submitting annual 
reports.[Footnote 15] 

Though many annual reports were missing from TMJ Concepts, FDA was able 
to review the two annual reports submitted by the sponsor in 2000 and 
2004. For both reports, TMJ Concepts included information related to a 
number of conditions of approval, such as providing data on its 
postmarket study and including a patient quality of life question in 
that study. In 2000, the sponsor did not comply with the condition of 
approval to separate data by patients' clinical histories, but did 
complete this in its 2004 annual report. Therefore, in 2004, TMJ 
Concepts addressed all conditions of approval except one--submitting 
annual reports each year. Although all conditions of approval were not 
met and FDA was not able to review 5 years of annual reports, FDA found 
that the 2000 and 2004 annual reports provided adequate data and no 
additional information was required of the sponsor for those two 
reports. 

FDA Required Some Sponsors to Take Additional Actions to Comply with 
Their Conditions of Approval: 

FDA evaluated information contained in the 13 annual reports it 
received and found that 7 reports--6 from TMJ Implants, Inc., (3 for 
the total joint implant and 3 for the partial joint implant) and 1 from 
Walter Lorenz--did not provide sufficient information to assess their 
compliance with conditions of approval.[Footnote 16] For 1 of the 7 
annual reports, FDA directed TMJ Implants, Inc., to submit new 
information about changes to the approved labeling and to the 
manufacturing processes for its total implant. FDA sent deficiency 
letters to the sponsors regarding the other 6 annual reports. These 
deficiency letters required the sponsors to address questions regarding 
the lack of certain data that relate to the safety and effectiveness of 
the devices, including patient history, patient follow-up, and adverse 
events. For example, in its 2006 annual report, Walter Lorenz was 
required to submit data on its postmarket clinical study. During the 
review of these data, the FDA review team identified concerns about 
data that were included in the report and sent a deficiency letter to 
the sponsor to resolve this issue. FDA officials discussed the 
deficiency letter with the sponsor and are waiting for a response. 

FDA took further steps to obtain compliance from TMJ Implants, Inc., 
which had not responded adequately to FDA's 2002 deficiency letter 
requesting additional information, following receipt of the sponsor's 
annual reports for its total and partial TMJ implants.[Footnote 17] 
Specifically, in 2002 FDA indicated that TMJ Implants, Inc. had not 
followed up with the required number of patients during its postmarket 
study. Also, the sponsor was not submitting adverse events, which it 
described in its annual reports, to FDA's Manufacturer and User 
Facility Device Experience Database (MAUDE).[Footnote 18] The sponsor 
reported that the reason for the implant removals was not specifically 
due to the failure of the implant and therefore concluded that they did 
not need to be reported as adverse events. However, after reviewing the 
2003 annual reports where there was still a lack of adverse event 
reporting, FDA issued a deficiency letter. This letter informed the 
sponsor that all removed implants should be reported to the MAUDE 
system. In addition, supplemental data were required to be submitted 
for the conditions of approval related to patient follow-up and adverse 
event reporting. After FDA's review of the sponsor's 2004 annual 
reports, the outstanding concerns from the 2002 and 2003 reports 
remained. For example, issues regarding lack of patient follow-up were 
unresolved. At the time of the 2004 annual reports, the sponsor 
submitted data for 75 out of a total of 183 patients for whom data 
should have been provided. The sponsor maintained that the events 
related to the removed devices were not caused by device failure or 
function and concluded that they did not require reporting to FDA. 
Subsequently, FDA took action on the 2004 annual reports by sending 
another deficiency letter to the sponsor. In addition, FDA required 
that the sponsor submit a complete account of all patients to clarify 
its analysis of patients who were lost to follow-up. 

According to FDA officials, the sponsor's response to these deficiency 
letters did not resolve the outstanding concerns. As a result, the 
review team raised the concerns with FDA's Office of Compliance and the 
sponsor was inspected from July 29 through August 11, 2003. During its 
inspection, FDA found that the sponsor's devices may have malfunctioned 
or caused or contributed to serious injuries. The inspection results 
also showed these adverse events had not been reported by the sponsor 
as required. In response to these findings, FDA issued a warning 
letter[Footnote 19] on February 24, 2004, requiring the sponsor to 
submit written medical device reports for specific adverse events 
detailed in the letter within 15 working days of receipt.[Footnote 20] 
When the sponsor did not adequately respond to the warning letter, FDA 
filed an administrative complaint on July 14, 2005, for civil monetary 
penalties, which resulted in a decision from an administrative law 
judge in favor of FDA on July 6, 2007. A separate decision is expected 
on the amount of the penalties to be assessed, after which either side 
may appeal. The FDA's Office of Regulatory Affairs instructed the 
review team not to pursue any deficiencies found in the sponsor's 
annual reports until the matter is resolved. Therefore, the review team 
has reviewed TMJ Implants, Inc.'s, 2005 and 2006 annual reports, but 
decisions on the sponsor's compliance with the conditions of approval 
are pending. 

Agency Comments: 

In commenting on a draft of this report, HHS provided clarification on 
the postmarket requirements that apply to approved devices and updated 
information concerning the administrative complaint for civil monetary 
penalties. We revised our report to reflect these comments. It also 
provided technical comments, which we incorporated, as appropriate. 
HHS's comments appear in appendix II. 

As arranged with your offices, unless you publicly announce the 
contents of this report earlier, we plan no further distribution of it 
until 30 days after its issue date. At that time we will send copies of 
this report to the Secretary of HHS, the Commissioner of the FDA, 
relevant congressional committees, and other interested parties. We 
will also make copies available to others upon request. In addition, 
this report will be available at no charge on GAO's Web site at 
[hyperlink, http://www.gao.gov]. 

If you or your staffs have any questions concerning this report, please 
contact me at (202) 512-7114 or crossem@gao.gov. Contact points for our 
Offices of Congressional Relations and Public Affairs may be found on 
the last page of this report. GAO staff who made major contributions to 
this report are listed in appendix III. 

Signed by: 

Marcia Crosse: 

Director, Health Care: 

[End of section] 

Appendix I: Concerns Left Unaddressed upon FDA Approval of TMJ 
Implants: 

While the Food and Drug Administration (FDA) addressed most concerns 
for each of the four temporomandibular joint (TMJ) implants we 
reviewed, we identified a number of concerns that were left 
unaddressed--concerns that were not offset or countered by a condition 
of approval or by FDA correspondence with the sponsor--upon approval. 
These unaddressed concerns fell into two of the four categories of 
concerns we identified previously: study protocol and other concerns. 
Table 2 lists the unaddressed concerns using the categories we 
established in table 1. 

Table 2: GAO Categorization of Concerns Left Unaddressed by FDA during 
the Premarket Approval Process for TMJ Implants: 

Concerns left unaddressed by FDA, sorted by sponsor: TMJ Concepts: Data 
on the effectiveness and survivability of the implant over time are not 
reliable because of flawed analyses; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Inadequate or inaccurate 
clinical study results. 

Concerns left unaddressed by FDA, sorted by sponsor: TMJ Concepts: Data 
on right and left side of the prostheses need to be analyzed 
separately; however, the sponsor did not provide data to allow for this 
analysis; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Inadequate or inaccurate 
clinical study results. 

Concerns left unaddressed by FDA, sorted by sponsor: TMJ Implants, Inc. 
(total implant): The data that demonstrate the performance of the 
implant will not diminish as a result of shipping and distribution are 
limited and questionable. In addition, there are specific concerns 
regarding the procedures that will be used for implants that will be 
shipped multiple times; 
Categories of concerns[A]: Other concerns; 
Types of concerns included in categories[B]: Unaddressed microbiology, 
packaging, and shelf-life issues. 

Concerns left unaddressed by FDA, sorted by sponsor: TMJ Implants, Inc. 
(total implant): More information is needed related to shelf life and 
packaging of the implant; 
Categories of concerns[A]: Other concerns; Types of concerns included 
in categories[B]: Unaddressed microbiology, packaging, and shelf-life 
issues. 

Concerns left unaddressed by FDA, sorted by sponsor: TMJ Implants, Inc. 
(partial implant: Data that indicate the performance of the implant 
will not diminish as a result of manufacturing processes must be 
submitted; 
Categories of concerns[A]: Other concerns; 
Types of concerns included in categories[B]: Incomplete sponsor 
manufacturing inspections. 

Concerns left unaddressed by FDA, sorted by sponsor: TMJ Implants, Inc. 
(partial implant: The sponsor has not yet submitted data related to 
outstanding microbiology, packaging, and shelf-life issues for its 
total implant, which it must do before approval of the partial implant; 
Categories of concerns[A]: Other concerns; 
Types of concerns included in categories[B]: Unaddressed microbiology, 
packaging, and shelf-life issues. 

Concerns left unaddressed by FDA, sorted by sponsor: TMJ Implants, Inc. 
(partial implant: Clarification and definition of patient inclusion 
criteria for the clinical study is needed to understand the clinical 
conditions of patients who received the implant; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Lack of patient history 
data. 

Concerns left unaddressed by FDA, sorted by sponsor: TMJ Implants, Inc. 
(partial implant: The sponsor has not provided a summary of 
preoperative conditions of patients enrolled in the study; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Lack of patient history 
data. 

Concerns left unaddressed by FDA, sorted by sponsor: Concerns left 
unaddressed by FDA, sorted by sponsor: The data do not indicate if 
patients enrolled in the clinical study have confounding conditions, 
which could affect results; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Lack of patient history 
data. 

Concerns left unaddressed by FDA, sorted by sponsor: Concerns left 
unaddressed by FDA, sorted by sponsor: The sponsor did not provide 
information on patients' past history, such as treatment history, to 
substantiate the use of an implant; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Lack of patient history 
data. 

Concerns left unaddressed by FDA, sorted by sponsor: Concerns left 
unaddressed by FDA, sorted by sponsor: The sponsor did not provide 
specific information about the nature of other treatments used with 
patients in the study; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Lack of patient history 
data. 

Concerns left unaddressed by FDA, sorted by sponsor: Concerns left 
unaddressed by FDA, sorted by sponsor: The use of broad diagnostic 
terms, such as internal derangement--displacement of the jaw joint--
makes it impossible to adequately identify patients who are candidates 
for this surgical treatment; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Inadequate or inaccurate 
clinical study results. 

Concerns left unaddressed by FDA, sorted by sponsor: Concerns left 
unaddressed by FDA, sorted by sponsor: The sponsor needs to provide 
more clearly defined indications and support for these indications; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Inadequate or inaccurate 
clinical study results. 

Concerns left unaddressed by FDA, sorted by sponsor: Concerns left 
unaddressed by FDA, sorted by sponsor: The sponsor has not provided 
data on the adverse events associated with the device; Categories of 
concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Inadequate or inaccurate 
clinical study results. 

Concerns left unaddressed by FDA, sorted by sponsor: Walter Lorenz; 
Categories of concerns[A]: [Empty]; Types of concerns included in 
categories[B]: [Empty]. 

Concerns left unaddressed by FDA, sorted by sponsor: Walter Lorenz: The 
sponsor generalizes data for all study subjects when they have 
different clinical history indicators; 
Categories of concerns[A]: Study protocol; 
Types of concerns included in categories[B]: Lack of patient history 
data. 

Source: GAO analysis of FDA documents. 

Notes: This table applies to the four TMJ implants approved since 
December 30, 1998. 

[A] We categorized concerns raised during the PMA approval process into 
four categories: study protocol, patient follow-up, engineering 
testing, and other concerns. 

[B] This column provides detail on the type of concern within the 
category to which the unaddressed concern relates. See table 1 for the 
four categories and the types of concerns we placed within these 
categories. 

[End of table] 

[End of section] 

Appendix II: Comments from the Department of Health and Human Services: 

Department of Health and Human Services: 
Office of the Assistant Secretary of Legislation: 
Washington, D.C. 20201: 

July 27, 2007:

Marcia Crosse: 
Director, Health Care: 
U.S. Government Accountability Office: 
Washington, DC 20548: 

Dear Ms. Crosse: 

Enclosed are the Department's comments on the U.S. Government Office 
Accountability Office's (GAO) draft report entitled: Medical Devices: 
FDA's Approval of Four Temporomandibular Joint Implants (GAO 07-996). 

The Department appreciates the opportunity to review and comment on 
this report before its publication. 

Sincerely, 

Signed by: 

Vincent J. Ventimiglia: 

Assistant Secretary for Legislation: 

General Comments Of The Department Of Health And Human Services (HHS) 
On The U.S. Government Office Accountability Office's (GAO) DRAFT 
Report Entitled: Medical Devices: FDA'S Approval Of Four 
Temporomandibular Joint Implants (GAO 07-996): 

1. Replace the last two sentences of the summary cover page with the 
following: 

This situation ultimately led FDA to inspect the sponsor's records and 
file an administrative complaint for civil monetary penalties against 
the sponsor for failure to file certain reports with FDA. On July 6, 
2007, the Administrative Law Judge ruled in favor of FDA. 

2. Replace the last paragraph on page 9 with the following: 

Once a device has been approved, the sponsor must comply with 
postmarket regulations and restrictions that apply to the device. 
Postmarket regulatory requirements that apply to devices include 
adverse event reporting and compliance with current Good Manufacturing 
Practices. Devices subject to premarket approval must also comply with 
annual report requirements, which include the requirement to report a 
summary of all changes to the device. FDA may also impose requirements 
in the Premarket Approval order; such requirements, known as postmarket 
approval or condition of approval requirements, apply specifically to 
the device that is the subject of the PMA. Conditions of approval can 
include requirements such as the continuation of a clinical study to 
collect additional data. Some conditions of approval do not expire, 
such as the conditions of reporting adverse events and submitting 
annual reports, while others are time limited, such as continuing a 
clinical study for a specified number of years after the approval of a 
device. 

3. On page 20, 6 lines from the bottom, replace "This matter has not 
yet... issued shortly" with the following: 

which resulted in a decision from the Administrative Law Judge in favor 
of FDA on July 6, 2007. TMJ Implants has thirty days in which the 
company may appeal this ruling. 


[End of section] 

Appendix III: GAO Contact and Staff Acknowledgments: 

GAO Contact: 

Marcia Crosse, (202) 512-7114 or crossem@gao.gov: 

Acknowledgments: 

In addition to the contact named above, Geraldine Redican-Bigott, 
Assistant Director; Deirdre Brown; Cathy Hamann; Julian Klazkin; 
Michaela M. Monaghan; and Sari B. Shuman made key contributions to this 
report. 

[End of section] 

Footnotes:  

[1] Medical devices may be deemed substantially equivalent to devices 
marketed prior to 1976 through the premarket notification process, 
referred to as the 510(k) process, which does not require the 
submission of additional information on the safety and effectiveness of 
the device. Substantial equivalence means, for example, that a device 
has the same intended use and same technological characteristics as a 
marketed device. 

[2] The TMJ Concepts implant PMA application was approved in July 1999, 
the TMJ Implants, Inc., total joint implant PMA application was 
approved in January 2001, the TMJ Implants, Inc., partial joint implant 
PMA application was approved in February 2001, and the Walter Lorenz 
implant PMA application was approved in September 2005. 

[3] Study protocol and patient follow-up concerns relate to the 
clinical studies sponsors must conduct to prove that their devices are 
safe and effective. Engineering testing refers to testing that is 
conducted on the TMJ implant to ensure it can withstand daily jaw 
activity. 

[4] One of the three sponsors, TMJ Implants, Inc., declined to speak 
with us. 

[5] We included FDA's monitoring of the conditions of approval, through 
the use of annual reports, in the scope of our work because these 
conditions relate to concerns raised in the PMA process. We excluded 
other FDA postapproval issues unrelated to concerns raised by FDA 
during the approval process. Many of FDA's postapproval activities for 
medical devices were reviewed recently in an Institute of Medicine 
report: Marilyn J. Field and Hugh Tilson, Safe Medical Devices for 
Children (Washington, D.C.: The National Academies Press, 2006), 
[hyperlink, http://www.nap.edu/catalog/11313.html] (downloaded Oct. 16, 
2006). In addition, FDA announced plans to improve postmarket programs 
for medical devices in November 2006. 

[6] While TMJ implants designed to treat temporomandibular joint and 
muscle disorders are classified as Class III devices, those that are 
used for a temporary period, such as to treat cancer patients with bone 
plate restructuring, are classified as Class II devices. Such devices 
present less risk than Class III devices. Class II TMJ implants have an 
intended use of 1 year or less. This review only includes the four 
Class III TMJ implants approved since December 30, 1998. 

[7] Submission of a PMA application is required for Class III devices 
unless the device was on the market prior to the enactment of the 
Medical Device Amendments of 1976 (Pub. L. No. 94-295) and FDA has not 
published a regulation requiring PMA submissions for the device. FDA 
issued regulations on December 30, 1998, requiring sponsors of all 
Class III TMJ implants to submit a PMA application for approval. 

[8] Each review team includes an engineer, statistician, and clinician 
who assess the PMA application. 

[9] DA regulations do not define "clinically significant results." See 
21 C.F.R. § 860.7(e)(1). However, an FDA official stated such results 
indicate that use of the device would have a positive effect on the 
disease being treated according to the standards of care for the 
related field. 

[10] For example, the review team may resolve application issues 
through meetings, phone calls, letters, or e-mails with the sponsor. 

[11] If the first level of management disagrees with the review team's 
recommendation regarding approval, the manager prepares a different 
recommendation and includes it in the review package that is forwarded 
to the second level of management, which makes the final decision 
regarding approval. 

[12] An FDA official told us that it is not uncommon for officials to 
write respectful disagreement memos when they feel strongly about their 
divergent views. He explained that this type of disagreement is an 
indicator of a healthy review process, in which officials are 
encouraged to think independently and thoroughly examine all aspects of 
a new device to help ensure its safety and effectiveness. 

[13] The regulations require these reports to be filed at intervals 
specified by FDA, and FDA has required reports annually. See 21 C.F.R. 
§ 814.82 (a)(7) (2006). 

[14] Survivability of the implant refers to the implant's ability to 
function in the jaw as originally intended over time. 

[15] The draft guidance, which was available for public comment for 90 
days after issuance, advises sponsors on how to best organize data and 
present the required information and what to expect from FDA in 
response to its annual report submission. This includes a new response 
format to standardize the review process and indicates that annual 
reports be reviewed by FDA within 90 days of receipt. 

[16] FDA received a total of 13 annual reports from the four TMJ 
implant sponsors: 2 annual reports from TMJ Concepts, 5 annual reports 
from TMJ Implants, Inc., for the total implant, 5 annual reports from 
TMJ Implants, Inc., for the partial implant, and 1 from Walter Lorenz. 

[17] TMJ Implants, Inc., submitted two annual reports each year after 
approval; one for the total implant and one for the partial implant. 

[18] Manufacturers are required to submit reports to FDA, which are 
included in its MAUDE database, whenever they receive information that 
reasonably suggests that one of their marketed devices (1) may have 
caused or contributed to a death or serious injury, or (2) has 
malfunctioned and that a recurrence would be likely to cause or 
contribute to a death or serious injury. Medical device user facilities 
and distributors also have responsibilities to report certain adverse 
events associated with medical devices or to maintain records of such 
events. In addition to these reports, FDA's MAUDE system includes 
reports that are voluntarily submitted by manufacturers, clinicians, 
and patients. 

[19] FDA may issue a warning letter to a sponsor if it believes that 
one or more of its products or practices violates the Federal Food, 
Drug, and Cosmetic Act, its implementing regulations, or other federal 
statutes. It is one of the principal methods used by FDA to achieve 
voluntary compliance with the applicable laws and regulations. 

[20] TMJ Implants, Inc., did not submit adverse event reports to the 
MAUDE database within 15 days of receiving the warning letter from FDA. 
However, from June 24, 2004, through March 27, 2007, 52 adverse events 
related to TMJ Implants, Inc., devices have been reported into the 
MAUDE database. Of those, 17 were reported by TMJ Implants, Inc., and 
all were determined by the sponsor not to be related to the device 
itself but to surgical complications, the surgeon, or other factors 
beyond the sponsor's control. 

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